A SECRET WEAPON FOR MUSCULAR DYSTROPHY THERAPIES VASANT KUNJ

not long ago, the antibiotic gentamicin continues to be tested in boys with DMD, about 10% of whom have inherited a dystrophin gene with a premature cease codon that halts the synthesis from the protein N-terminal to the dystroglycan binding location. Gentamicin suppresses chain termination, allowing some whole-length dystrophin being created. This